What are the trends, challenges and opportunities with niche and rare disease drug markets?

Niche and rare disease drugs are experiencing transformative growth, with revolutionary, premium-priced therapies entering the marketplace. DRG’s Niche & Rare Disease Landscape & Forecast (N&R DL&F) module provides a comprehensive assortment of market segments that offer the greatest potential.

Assess new areas of growth

DRG’s Niche & Rare Disease Landscape & Forecast (N&R DL&F) module is the industry’s most comprehensive source of vital disease-specific business and market intelligence. Our portfolio includes detailed assessments of more than 20 niche and rare disease markets, spanning across several therapeutic areas.


Understanding built on primary research

With DRG’s Niche & Rare DL&F module, you will be able to:

  • SIZE POPULATIONS AND MONITOR EPIDEMIOLOGICAL TRENDS.
  • KNOW THE STRENGTHS, WEAKNESSES, AND POSITIONING OF CURRENT TREATMENTS.
  • LEARN THE TOP UNMET NEEDS AND CORRESPONDING OPPORTUNITIES.
  • ASSESS THE LINE-UP OF EMERGING THERAPIES, FROM EARLY TO LATE PHASE.
  • EVALUATE MARKET POTENTIAL FOR YOUR PIPELINE ASSETS — AND THOSE OF YOUR COMPETITORS.
  • OPTIMIZE YOUR LONG-TERM DISEASE/DEVELOPMENT STRATEGY

Lose nothing in translation

For each of the niche and rare diseases covered, access a 10-year out, epidemiology-based, pharmaceutical market forecast for key therapies in the United States and the EU5 – France, Germany, Italy, Spain, and the United Kingdom.


“The niche & rare DL&F content often provides the first or only thorough and deep analysis of a nascent disease market, helping frame the discussion and identify viable paths forward. The Niche & Rare DL&F offering informs clients of the unique challenges in treating each niche and rare disease from the perspective of thought leaders, and highlights the commercial opportunities, as well as barriers and hurdles associated with them, to aid developers to successfully penetrate these markets.”

DERMATOLOGY

Atopic Dermatitis/Eczema

HEMATOLOGICAL MALIGNANCIES

Acute Lymphoblastic Leukemia
Acute Myeloid Leukemia
Hodgkin’s Disease
Myelodysplastic Syndromes
Myelodyfibrosis

HEMATOLOGY

Beta Thalassemia
Hemophilia
Idiopathic Thrombocytopenic-
Purpura (ITP)
Sickle Cell Disease

METABOLIC

Acromegaly
Amyloidosis
Non-alcoholic Steatohepatitis (NASH)

NEUROLOGY

Autism
Amyotrophic Lateral Sclerosis
Friedreich’s Ataxia
Huntington’s Disease
Muscular Dystrophy
Spinal Muscular Atrophy

RESPIRATORY

Cystic Fibrosis
Idiopathic Pulmonary Fibrosis

RHEUMATOLOGY

Juvenile Idiopathic Arthritis
Systemic Sclerosis (Scleroderma)
Sjögren’s Syndrome

SOLID TUMORS

Bladder Cancer
Glioma
Hepatocellular Carcinoma
Pancreatic Cancer
Small Cell Lung Cancer
Thyroid Cancer

TRANSPLANT

Graft Versus Host Disease

VIRAL INFECTIONS

Cytomegalovirus (CMV)
Respiratory Syncytial Virus (RSV)

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